S
Spinal muscular atrophyW
Spinal muscular atrophy
AveXisW
AveXis
A
BiogenW
Biogen
BranaplamW
Branaplam
B
Johann Hoffmann (neurologist)W
Johann Hoffmann (neurologist)
Ionis PharmaceuticalsW
Ionis Pharmaceuticals
C
NusinersenW
Nusinersen
OlesoximeW
Olesoxime
D
RisdiplamW
Risdiplam
SMN1W
SMN1
E
SMN2W
SMN2
Spinal muscular atrophiesW
Spinal muscular atrophies
F
Survival of motor neuronW
Survival of motor neuron
Guido WerdnigW
Guido Werdnig